Human pathology

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CDG1B

CDG-Ib, congenital disorder of glycosylation type Ib, carbohydrate-deficient glycoprotein syndrome type Ib, phosphomannose isomerase deficiency

Congenital disorder of glycosylation type Ib (CDG Ib, CDG1B) is caused by mutation in the gene encoding mannosephosphate isomerase (MPI) (MIM.154550). Autosomal recessive.

Synopsis

- congenital hyperinsulinism (hyperinsulinaemic hypoglycaemia) (10484808, 12872847)
- hepatic fibrosis
- failure to thrive
- hepatomegaly
- hepatic fibrosis
- cirrhosis
- hepatic failure
- vomiting
- diarrhea
- villous atrophy
- lymphangiectasia
- protein-losing enteropathy
- hypotonia
- hyperinsulinemic hypoglycemia
- anti-thrombin III deficiency
- thrombosis
- factor XI deficiency
- bleeding episodes

- Abnormal isoelectric focusing of serum transferrin, type I pattern
- Phosphomannose isomerase deficiency in leukocytes, fibroblasts, or liver
- Hypoalbuminemia

- Onset of symptoms 2-12 months
- Responsive to oral mannose therapy

Etiology

- phosphomannose isomerase deficiency