Human pathology

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dolichol phosphate biosynthesis

Dolichol phosphate is involved in several glycosylation reactions, such as N-glycosylation, glycosylphosphatidylinositol (GPI)-anchor biosynthesis, and C- and O-mannosylation.

Pathology

- CDG1M or dolichol kinase (DK1) deficiency (17273964)

  • DK1 is responsible for the final step of the de novo biosynthesis of dolichol phosphate.
  • Affected patients present with a very severe clinical phenotype, with death in early infancy. Two of the patients died from dilatated cardiomyopathy.

References

- Kranz C, Jungeblut C, Denecke J, Erlekotte A, Sohlbach C, Debus V, Kehl HG, Harms E, Reith A, Reichel S, Grobe H, Hammersen G, Schwarzer U, Marquardt T. A defect in dolichol phosphate biosynthesis causes a new inherited disorder with death in early infancy. Am J Hum Genet. 2007 Mar;80(3):433-40. PMID: 17273964